Startseite Kongressberichte & Archiv Archiv 2018 American Society of Hematology (ASH) 60th Annual Meeting and Exposition Thalassemia and Globin Gene Regulation

Maria Domenica Cappellini, et a.

163 The Believe Trial: Results of a Phase 3, Randomized, Double-Blind, Placebo-Controlled Study of Luspatercept in Adult Beta-Thalassemia Patients Who Require Regular Red Blood Cell (RBC) Transfusions

Conclusions from the Abstract: Treatment with luspatercept resulted in significant reductions in RBC transfusion burden in adults with transfusion-dependent β-thalassemia. Luspatercept was generally well tolerated in this patient population.